The trial follows Sidra Medicines launch of its Clinical Trials Program, aimed at offering a new lease of hope to children with rare and complex diseases ...

Prevent Blindness announces its fourth annual Geographic Atrophy Awareness Week, December 2 to 8, 2024. The organization ...

Early diagnosis of rare diseases like Spinal Muscular Atrophy (SMA) is crucial for managing symptoms and improving quality of ...

One major health challenge in the aging population is the decline in muscle mass, strength and function (otherwise known as ...

Mumbai: Impact Guru, a popular crowdfunding platform in India, has become the centre of controversy following an FIR against ...

Assisted dying could be legalised in England and Wales after a historic vote saw proposed legislation clear its first hurdle ...

Luis's wheelchair is part of his everyday life with spinal muscular atrophy and he faces challenges with mobility and living ...

Children with severe SMA have substantial loss of motor and sensory neurons in the thoracic region of the spinal cord, a ...

Scientists studied 188 people related to someone with ALS caused by a C9ORF72 mutation to identify markers of disease risk in ...

Biohaven's pipeline includes Troriluzole for SCA, BHV-2100 for migraines, and Taldefgrobep Alfa for SMA. See why BHVN stock ...

A new study has revealed that a lesser-known symptom of dementia could have a significant impact on driving ability ...

The authors emphasize the value of subgroup analyses for tracking patterns in spinal muscular atrophy (SMA), as opposed to ...