The voluntary model, led by the Center for Medicare and Medicaid Innovation, aims to test outcomes-based agreements for cell and gene therapies. CMS says that the model will increase access for ...

Upon deletion of the ALAS2 gene, the researchers subsequently observed classic symptoms of XLSA like anemia and enlargement of the spleen. The model also allowed the researchers to note features ...

For this heart failure model, heart failure generally leads to death within a few months. But all four pigs that received the gene therapy in their heart cells survived for six months, the ...

New gene therapy reverses heart failure in large animal model. ScienceDaily . Retrieved January 2, 2025 from www.sciencedaily.com / releases / 2024 / 12 / 241210115612.htm ...

Upon deletion of the ALAS2 gene, the researchers subsequently observed classic symptoms of XLSA like anemia and enlargement of the spleen. The model also allowed the researchers to note features of ...

2024 — Researchers restored hearing in preclinical mouse models with a specific form of inherited deafness called DFNA50 caused by mutations in microRNA, by ... June 13, 2024 — A viral gene ...

A new gene therapy can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the amount of blood the heart can pump and dramatically improves ...

The study highlights the iFlpMosaics toolkit's utility across different experimental setups, detailing how it allows scientists to track the effects of single or multiple gene deletions within the ...

At the University of Utah, scientists used a new gene therapy that was shown to reverse ... this therapy will be effective outside animal models and to identify any "downstream effects." ...

Gene Park is a reporter for The Washington Post, covering video games and gaming culture. He joined The Post in 2015 as audience editor, and is a former reporter in the West Coast and Pacific region.