Vertex's Cystic Fibrosis Drug Alyftrek Gets FDA Approval
(RTTNews) - Vertex Pharmaceuticals Inc. (VRTX) Friday announced that the U.S. Food and Drug Administration (FDA) has approved Alyftrek for treatment of cystic fibrosis.
Vertex Gains FDA Approval for Cystic Fibrosis Drug Alyftrek
Alyftrek is Vertex's fifth CFTR modulator to secure FDA approval. It is also under regulatory review in the European Union, the United Kingdom, Canada, Switzerland, Australia and New Zealand. Write to ...
MarketWatch2 天
Vertex Gets Expanded FDA Approval for Cystic Fibrosis Treatment
The medicine, called trikafta, can treat cystic fibrosis patients who have at least one F508del mutation in the transmembrane conductance regulator gene or a mutation that is responsive to trikafta ...
Medscape6 天
Cystic Fibrosis Transmembrane Conductance Regulator–Modifying Medications
combined groups: −5.4 mV (p < 0.001) CF = cystic fibrosis; FEV 1 = forced expiratory volume in 1 second. The classes of cystic fibrosis transmembrane conductance regulator (CFTR) mutations.
Nature4 年
Finding a path to a cure for cystic fibrosis
CF often arises from mutations that make the cystic fibrosis transmembrane conductance regulator (CFTR) protein misfolding and malfunction, causing thick mucus to aggregate in the lungs while also ...
Vertex' Trikafta Gets Expanded FDA Approval For Cystic Fibrosis Treatment
Vertex Pharmaceuticals (VRTX) said Friday the U.S. Food and Drug Administration expanded its approval of a cystic fibrosis treatment, ...
Nature4 年
Liver disease in cystic fibrosis: prevalence and risk factors
severity of pulmonary disease and genotype for cystic-fibrosis transmembrane conductance regulator were not. Although half of the patients with liver disease were treated with ursodeoxycholic acid ...
Leader-Post1 个月
Cystic fibrosis drug now available to more people in Saskatchewan
The medication is a CF transmembrane conductance regulator (CFTR) modulator therapy, made to correct the malfunctioning protein made by the CFTR gene. Cystic Fibrosis Canada (CFC) is celebrating ...
Kaleido Scope5 年
CFTR Protein Production Core
The CFTR Protein Distribution Core offers high-quality, full-length recombinant cystic fibrosis transmembrane conductance regulator (CFTR) proteins expressed in and purified from mammalian cells. Wild ...
Yahoo Finance1 个月
ReCode to secure funds for cystic fibrosis gene correction treatments
The initiative, conducted in collaboration with Intellia Therapeutics, aims to develop new treatments for cystic fibrosis ... cystic fibrosis transmembrane conductance regulator (CFTR) modulators.
Vertex Announces US FDA Approval of ALYFTREK™, a Once-Daily Next-in-Class CFTR Modulator ...
Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today announced that the U.S. Food and Drug Administration (FDA) has ...
Medical Xpress26 天
Cystic Fibrosis
CF is caused by a mutation in the gene for the protein cystic fibrosis transmembrane conductance regulator (CFTR). This gene is required to regulate the components of sweat, digestive juices ...