mRNA-3927 is under development for the treatment of propionic acidemia in pediatrics. It is developed based on messenger RNA expression and N2GL formulation platform. The therapeutic candidate ...

Sandra A. Banta-Wright, MN, RNC, NNP; Robert D. Steiner, MD Neonates with profound and prolonged hyperammonemia with coma due to urea cycle defect will have had a neurological insult to the brain ...