Breakthrough gene therapy offers new hope to child with muscular dystrophy
Monroe Carell was a natural fit to offer the new therapy. Its multidisciplinary DMD Clinic, co-directed by Burnette, Soslow ...
Is your child not crawling? They could have THIS rare disease
Early diagnosis of rare diseases like Spinal Muscular Atrophy (SMA) is crucial for managing symptoms and improving quality of ...
Cuba Headlines6 天
Child with Muscular Dystrophy Denied Housing by Cuban Authorities
A Cuban teenager suffering from Duchenne muscular dystrophy, a degenerative disease that leaves him bedridden, reliant on ...
WebMD1 年
Exercises for Spinal Muscular Atrophy
For children with SMA, assistive devices -- walkers, wheelchairs, standers, and more -- are the key to staying active. Learn which ones may help your child.
BBC1 年
Muscular dystrophy: Child racks up 1,200 miles a month for treatment
Lucy Vers' five-year-old son Elliot has Duchenne, the most common and severe form of muscular dystrophy Parents of children living with muscular dystrophy say better expertise is needed in Wales ...
Nature7 年
Medical Ethics: Genetic Testing and Spinal Muscular Atrophy
The mutation that causes Spinal Muscular Atrophy (SMA ... be faced with many decisions regarding the health of affected children and the well-being of other family members. Some of these families ...
来自MSN9 个月
‘Finally time to go home’: Child with spinal muscular atrophy leaves hospital after months
His challenges started soon after he was born when newborn screening led to a diagnosis of a genetic disorder called spinal muscular atrophy ... referred to Akron Children’s Hospital where ...